Explore information about emerging therapies and clinical trials for mitochondrial disease. Find information about therapies in development, understand the clinical trial process and stay up to date with research advances.
Active mito trialsÂ
Approved therapies
Considering a clinical trial?
Learn how clinical trials work, what participation may involve, and what to consider before deciding whether taking part is right for you or someone you care for.
Find therapies and trials
Researchers around the world are investigating new therapies for mitochondrial disease.
Use our Therapy Finder to:
- explore therapies currently in development
- learn which types of mito they may target
- find information about associated clinical trials.
Increasing clinical trials for mito in Australia: our role
While new treatments are emerging worldwide, Australians are at risk of missing out. Access to clinical trials and emerging therapies remains limited.
The challenge now is clear. As global progress accelerates, Australia must strengthen its clinical trial capacity and connections to ensure people living with mito can benefit.
Through our 10-year action plan, Mito Foundation is building a trial-ready community, strengthening research capacity, and supporting collaboration across the sector.
We also track global clinical trial activity and provide clear information to help people understand their options and take part with confidence.
Powering progress: A plan to increase clinical trials for mitochondrial disease in Australia
Powering Progress: one year on
Helpful resources
Powering progress: The future of clinical trials for mito
VideoMito Foundation and Research Australia hosted this event to discuss increasing clinical trials for mitochondrial disease (mito) in Australia. Speakers included people with lived experience and leaders in the field. Together, they brought wide-ranging life experiences and professional insights. They discussed:
- the clinical trial process
- why some trials not coming to Australia and what can we do to change this
- how we can work together to shape the future of clinical trials.
The event was recorded on 16 April 2025.
Learn more about our plan to increase clinical trials for mito in Australia.
